Executive Committee (EC): Project steering group
| Name and Title | Study Function | 
|---|---|
| Fredrik Piehl, MD, PhD Consultant Neurologist | Coordinating Principal Investigator | 
| Anders Svenningsson, MD, PhD Consultant Neurologist | Principal Investigator | 
| Thomas Frisell, PhD Biostatistician, Karolinska Institutet | Responsible statistician | 
| Ingrid Kockum, PhD Bioinformatician, Karolinska Institutet | Responsible for data handling | 
| Anna Fogdell-Hahn Immunologist, Karolinska Institutet | Project manager and responsible for laboratory testing of ADA | 
| Annette Langer-Gould, MD, PhD Kaiser Foundation Research Institute (Pasadena, USA) | Principal Investigator | 
| Suvi Virtanen Epidemiologist, Karolinska Institutet | Project coordinator and site monitor | 

 Percentage RTX use off all ongoing DMD's

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